About Fabry Disease
Recent Posts
- Jeff’s Journey With Fabry Disease
- Eye vessel abnormalities may signal heart disease in Fabry patients
- We need more oral Fabry disease treatment options that reduce pain
- AMT-191 shows promise, but safety concerns prompt dosing pause
- Guest Voice: Believe us when we say we’re having a bad day
- Sangamo starts FDA submission seeking approval of Fabry gene therapy
- Managing my hypertension has required some trial and error
- Long-term use of lucerastat may protect kidneys in Fabry: Trial data
- Seeking good news as symptom relief eludes my children
- Brain health remains stable for Fabry patients on Galafold: Study