A Fabry disease diagnosis for a woman in Portugal came only after she had a stroke in her early…
Articles by Marisa Wexler, MS
Throughout 2024, the team at Fabry Disease News brought our readers all the latest updates on research related to …
The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to EXG110, an experimental gene therapy for…
Amicus Therapeutics and Teva Pharmaceuticals have struck a deal that will allow the latter to sell a generic version…
Programs that systematically tested for Fabry disease in nearly 1,000 people with chronic pain at centers in France led…
An international team of scientists has developed a novel algorithm that may help identify people with Fabry disease based…
Despite available treatments, many people with Fabry disease still experience symptoms that can affect their quality of life, a…
People with Fabry disease have higher-than-normal levels of three inflammatory markers in their blood, according to a recent study.
A woman with Fabry disease was found to have two co-occurring disorders — a heart condition called dilated cardiomyopathy…
The U.S. Food and Drug Administration (FDA) has advised Sangamo Therapeutics that positive results from a single well-controlled…