Testing family members of people diagnosed with Fabry disease can identify new individuals with the condition and improve their…
Articles by Marisa Wexler, MS
The European Commission (EC) is expected to decide whether to approve PRX-102 (pegunigalsidase alfa) for adults with Fabry…
People with Fabry disease often have impairment in the nerves that help regulate heartbeat, which may serve as a…
More than one in 10 people with Fabry disease have a form of swelling called lymphedema, a recent study…
The U.S. Food and Drug Administration (FDA) has placed a hold on the 4D-310 clinical program, an experimental gene therapy…
One year after treatment with 4D-310, an experimental gene therapy for Fabry disease, measures of heart health have improved…
A program that screened nearly 500 men with implanted pacemakers for Fabry disease found that none of them had…
ISU303, an experimental enzyme replacement therapy for Fabry disease, showed a good safety profile and some promising signs of…
One-time treatment with ST-920 (isaralgagene civaparvovec), an experimental gene therapy being developed by Sangamo Therapeutics, continues to be generally…
Implementing nationwide screening programs for Fabry disease in people with a heart condition called hypertrophic cardiomyopathy (HCM) may help…