Recent Posts
- FDA clears uniQure trial of AMT-191 gene therapy in Fabry patients
- How expressing gratitude causes our happiness to grow
- 13 essential ways I stay healthy with Fabry disease
- First patient dosed in Phase 2 study of oral therapy candidate AL01211
- Low muscle mass may be early sign of Fabry disease in children
- 4DMT, FDA agree to lift clinical hold on Fabry gene therapy 4D-310
- Nurses and patients work together to make home infusions successful
- Patients’ anti-PEG antibodies may not block effects of Elfabrio: Study
- Most patients experience sleep-related disorders: Review study
- Many Fabry families, including mine, benefit from Make-A-Wish