Ryan Golley,  —

Recent Posts

• FDA clears uniQure trial of AMT-191 gene therapy in Fabry patients
• How expressing gratitude causes our happiness to grow
• 13 essential ways I stay healthy with Fabry disease
• First patient dosed in Phase 2 study of oral therapy candidate AL01211
• Low muscle mass may be early sign of Fabry disease in children
• 4DMT, FDA agree to lift clinical hold on Fabry gene therapy 4D-310
• Nurses and patients work together to make home infusions successful
• Patients’ anti-PEG antibodies may not block effects of Elfabrio: Study
• Most patients experience sleep-related disorders: Review study
• Many Fabry families, including mine, benefit from Make-A-Wish