Fabry Disease News
Recent Posts
- AMT-191 shows promise, but safety concerns prompt dosing pause
- Guest Voice: Believe us when we say we’re having a bad day
- Sangamo starts FDA submission seeking approval of Fabry gene therapy
- Managing my hypertension has required some trial and error
- Long-term use of lucerastat may protect kidneys in Fabry: Trial data
- Seeking good news as symptom relief eludes my children
- Brain health remains stable for Fabry patients on Galafold: Study
- Timing of Fabry enzyme therapy linked to long-term heart stability
- Gene mutation, kidney health linked to lower stroke risk in Fabry: UK Study
- Canada approves ERT Elfabrio for adults with Fabry disease