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November 12, 2021 News by Marta Figueiredo, PhD

One-time AVR-RD-01 Gene Therapy Safe Up to 4.5 Years, Trials Report

A single dose of Avrobio’s investigational gene therapy AVR-RD-01 continues to show a favorable safety and tolerability profile for up to 4.5 years in adolescents and adults with Fabry disease, according to latest data from Phase 1 and Phase 2 clinical trials. Notably, up to 3.5-year data previously showed the…

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