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December 2, 2022 News by Lindsey Shapiro, PhD

Venglustat Lowers Gb3 With No Signs of Disease Progression in Trial

Daily treatment with the investigational oral therapy venglustat in men with Fabry disease led to significant reductions in globotriaosylceramide (Gb3 or Gl-3) — the fatty molecule that accumulates to toxic levels in the disease — and no signs of disease progression. That’s according to up to three years…

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