AVROBIO, a biotechnology company developing single-dose gene therapies for rare diseases, announced positive preliminary data for its Phase 1/2…
Articles by Diogo Pinto
Inflammation of the heart, known as myocarditis, is found in more than half of patients with Fabry disease cardiomyopathy…
The U.S. Food and Drug Administration has granted accelerated approval to Galafold (migalastat) 123 mg capsules to treat adults with a confirmed…
A handheld imaging device may help physicians confirm a diagnosis of Fabry disease in patients, according to a case…
Kidney injury associated with Fabry disease significantly varies among patients. Family members with unknown kidney disease should consider Fabry disease…