Author Archives: Vanda Pinto PhD

Fabrazyme Biosimilar Marketed in Japan Under New Agreement

JCR Pharmaceuticals and Sumitomo Dainippon Pharma have teamed up to market and commercialize in Japan agalsidase beta BS, a biosimilar of Fabrazyme, an already approved treatment designed to replace a critical enzyme missing in people with Fabry disease. According to a company press release, “This…

Experimental Gene Therapy May Be Safe and Effective, Early Data Shows

Experimental gene therapy 4D-310 continues to be generally safe and has effectively increased enzyme alpha-galactosidase (Gal A) blood levels in the first three patients enrolled in 4D Molecular Therapeutics’s clinical trial. These results were announced in the presentation “An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in…